美国食品药品监督管理局（FDA）已向 Applied Therapeutics 公司发出了一份完整回复函（CRL），涉及 govorestat 用于治疗经典半乳糖血症的新药申请（NDA）。 该 NDA 包含 1/2 期 ...

Galactosemia (G) is due to either partial or complete deficiency of the enzyme galactose-1-phosphate uridyl transferase (Ts). In females with G, there is a high incidence of premature ovarian failure.

In the phase III ACTION-Galactosemia Kids study in children with ... Allogene Therapeutics’ estimates for loss per share have narrowed from $1.40 to $1.35 for 2024, and that for 2025 has ...

Looking for reliable medications to treat 'Galactosemia'? This page offers a detailed resource for the most up-to-date treatment options, including both generic and brand-name medications.

Considering taking supplements to treat galactosemia? Below is a list of common natural remedies used to treat or reduce the symptoms of galactosemia. Follow the links to read common uses ...

Applied Therapeutics' (APLT) lead drug candidate, govorestat, likely faces "significant" uncertainty in potentially treating galactosemia after the US Food and Drug Administration rejected the ...