Galactosemia (G) is due to either partial or complete deficiency of the enzyme galactose-1-phosphate uridyl transferase (Ts). In females with G, there is a high incidence of premature ovarian ...
Looking for reliable medications to treat 'Galactosemia'? This page offers a detailed resource for the most up-to-date treatment options, including both generic and brand-name medications.
In the phase III ACTION-Galactosemia Kids study in children with galactosemia aged 2-17 years, govorestat improved daily activities, behavior, cognition, fine motor skills and tremor. It also ...
The submission included clinical data from the Phase III ACTION-Galactosemia Kids study in kids aged two to 17 years; the Phase I/II ACTION-Galactosemia study in adults; as well as preclinical ...