Gene-transfer approaches are based upon the simple concept that if a disease is due to a recessive loss-of-function mutation in a single gene, then adding back the wild-type gene should restore ...

In collaboration with colleagues from international partner institutions, researchers at the University of Cologne have ...

A team of researchers at the Helmholtz Institute for Pharmaceutical Research Saarland (HIPS) has now developed a genetic method that leverages a natural bacterial mechanism for the transfer of ...

“A significant number of individuals with focal epilepsy are refractory to all anticonvulsants, and there is a clear unmet clinical need which justifies potential risky procedures like resective ...