Hosted on MSN3d
CHOP doctors named 'Disruptors of the Year' for groundbreaking sickle cell gene therapy
The Philadelphia Citizen is recognizing CHOP doctors Alexis Thompson and Dr. Stephan Grupp with the 'Disruptors of the Year' ...
Sickle cell gene therapies are gaining steam
Nearly a year after new sickle cell gene therapies were approved, CNBC's Bertha Coombs reports a small number of patients are ...
Harvard Medical School3d
Creating the World’s First CRISPR Medicine, for Sickle Cell Disease
In December 2023, through the development efforts of CRISPR Therapeutics and Vertex Pharmaceuticals, their decades-long ...
Medscape11d
Sickle Cell Trait Widely Misinterpreted As Cause of Death
A new review and policy statement underscore the inaccuracy of sickle cell trait as a cause of death on autopsies.
14-Year-Old Boy Discovers He Needs a Heart Transplant During a Family Vacation After Experiencing This Symptom (Exclusive)
On a family vacation, 14-year-old Jaden Hartley discovered he needed a heart transplant after experiencing this symptom. Now ...
Sickle cell disease is a genetic disorder that causes lifelong suffering—here's what you need to know
Right now, approximately 20 billion red blood cells are busy traveling through your blood vessels. They are delivering oxygen ...
Once high-flying Bluebird Bio sells itself to private equity after tough times for the gene therapy maker
Bluebird Bio will sell itself to private equity firms Carlyle and SK Capital for about $30 million, the company said Friday.
FiercePharma2d
Once valued at $10B, bluebird bio sold to private equity firms for $29M
There is a catch. If the private equity firms can boost sales of bluebird’s three gene therapies to $600 million—over any ...
Health Affairs12d
An Agenda For Sickle Cell Disease Research That Encompasses Lived Experience
As treatment and care continues to evolve, we must ensure that people living with this disease are able to advocate for ...
Madison3654d
Urban League of Greater Madison, American Red Cross will partner for Sickle Cell Blood Drive on Feb. 22
The Urban League of Greater Madison and The American Red Cross will host a Sickle Cell Awareness Blood Drive on Saturday, Feb ...
The Daily Monitor on MSN8d
Govt orders premarital sickle cell testing to curb disease burden
“We still have a serious challenge with sickle cell disease, which contributes to 20% of under-five mortality every year.