Title: Impact of the Enzyme Replacement Therapy, INZ-701, in Children with ENPP1 Deficiency: Experience from an Expanded Access Program Presentation Number: 10 – Poster Session Date: Saturday, ...

In India, 32 patients, diagnosed with this condition by the Centres of Excellence (CoEs), have registered themselves with the ...

The enzyme replacement therapy (ERT) market is projected to grow significantly, rising from US$ 10,707.6 million in ...

If you often feel bloated fatigued or struggle with weak hair and nails despite eating enough protein your body might not be digesting it properly Read this article to know signs of protein indigestio ...

Researchers identified genetic variants affecting sucrase, a key digestive enzyme, linked to IBS risk and symptom severity.

Acute respiratory infections (ARIs) are a common cause of illness in children younger than 16 years and adults older than 65 ...

With thyroid disease, the effects of "too high or too low" are both problematic, and there is no natural therapy that can simultaneously address both conditions. Herbs for Iodine Deficiency Your body ...

The Isaac Foundation has been the recipient of $2,500 from the Blessings to You Centre, Palmerston. In June of 2011, at the ...

BioMarin's gene therapy pipeline has had setbacks, including a three-year delay in US approval of Roctavian and stalled development of PKU gene therapy BMN 307 as the Food and Drug Administration ...

"The FDA is dedicated to supporting new drug development for rare diseases including very rare metabolic diseases like cerebrotendinous xanthomatosis," said Janet Maynard, M.D., M ...

The approval makes chenodiol—already cleared for decades to treat radiolucent gallstones under the brand name Chenodal—the ...