Cellular therapy, according to the Dana-Farber Cancer Institute, is designed to improve the immune system’s ability to fight ...

Dec. 10, 2024 — In a single IV injection, a gene therapy targeting cBIN1 can reverse the effects of heart failure and restore heart function in a large animal model. The therapy increases the ...

Mía had dystrophic epidermolysis bullosa, better known as butterfly skin due to the extreme fragility of this tissue in ...

Development strategies designed to reduce the unknowns so that cell and gene therapy innovators can develop robust processes efficiently.

The company made its debut last year with a $51 million Series A and a licensing agreement with Astellas for a gene therapy candidate (KT430) for X-linked myotubular myopathy. Shortly after that ...

That’s important because thousands of mutations across more than 50 genes have been associated with RP, so a gene therapy that targets just one mutation would only work in a subset of patients.

A new Oregon Health & Science University and Weill Cornell Medicine co-authored study provides critical insight for the ...

“The KickStart Grant Awards help de-risk these technologies by establishing a collaboration agreement between the startup ...

Haseeb Ahmad brings over 25 years of leadership experience in life sciences, most recently serving as President of Novartis ...

Jonathon Whitton, AuD, PhD, VP, auditory global program head, Regeneron, discusses how key regulatory designations, such as the FDA's Regenerative Medicine Advanced Therapy designation, facilitate ...

“The real stroke of brilliance is the notion that you make the cell younger, and then it would be more resilient to injury,” ...