The FDA has approved Alnylam’s gene silencing drug Oxlumo, the first treatment ... FDA-approved a year ago for acute hepatic porphyria, costs $575,000 per year at full price in the US, although ...

In 2018, Alnylam's Onpattro (patisiran) became the first ever RNAi drug to be approved by the ... for acute hepatic porphyria (AHP) and Oxlumo (lumasiran) for primary hyperoxaluria type 1 (PH1).

Treatment strategies range from outpatient dietary advice and antiemetic drugs to hospitalization and intravenous (IV) fluid replacement in persistent or severe cases. Alternative methods ...

variegate porphyria, xeroderma pigmentosum, arterial ischaemic stroke, DNA repair, Parkinson's disease and more.

Drug discovery is the process through which potential new medicines are identified. It involves a wide range of scientific disciplines, including biology, chemistry and pharmacology. The field of ...

Here, azadirachtin is co-assembled with plant secondary metabolites for efficient drug delivery, demonstrating pest management, the activation of plant defensive capacity, while increasing the ...

The hospital gave me no cost information, yet weeks later, I received a $2,000 bill that I couldn't afford to pay.

For example, you might find one on the floor and need to figure out what it is. Or maybe you just picked up your new prescription from the pharmacy and want to confirm it's the right drug. When ...

In addition to treating symptoms, prokinetic drugs could potentially improve glycemic control in diabetic gastroparesis by allowing a more predictable absorption of nutrients, matched to the ...

A New Psychoactive Substance (NPS) is a substance of abuse, either in a pure form or a preparation, that is not controlled by the 1961 Single Convention on Narcotic Drugs or the 1971 Convention on ...