Total Revenue of $560 million, exceeding guidanceCrysvita® revenue of $410 million and Dojolvi® revenue of $88 million2025 Financial ...

This is one of 22 cutting-edge projects selected to share in a total of $8.1 million in grants raised through the Eagles ...

By studying the gene UBE3A, which plays a role in protein breakdown in neurons, Levine's team hopes to identify ways to correct or silence problematic genes. Their research could one day lead to ...

Dr. Eric Levine’s cutting-edge autism research at UConn School of Medicine is reprogramming the donated skin or blood cells of autism-linked Angelman or Dup15q syndrome patients to develop them in the ...

His research team has already shown there is a driver gene of UBE3A, which breaks down other cellular proteins in neurons, which can be either under- or overexpressed in the Angelman and Dup15q ...

A gene regulatory network is a set of genes, or parts of genes, that interact with each other to control a specific cell function. Gene regulatory networks are important in development ...

(MENAFN- PR Newswire) The team at UCLA is further developing this gene therapy approach in which a patient's own blood stem cells can be modified to add a healthy copy of the UBE3A gene that is ...

AUSTIN, Texas, Jan. 30, 2025 /PRNewswire/ -- Dr. Roger Hollis from the University of California, Los Angeles, project scientist from the laboratory of Dr. Donald Kohn, a world leader in ...

Donald Kohn, a world leader in developing gene replacement therapies using blood stem cells, has been awarded a $5.8 million translational research award from the California Institute for ...