The management of achondroplasia, given its systemic nature, requires multidisciplinary cooperation to maximize outcomes. Achondroplasia is a genetic skeletal dysplasia that affects the development ...

The R&D head is looking for "clever science," which Friberg said is readily apparent in BioMarin’s recent research pact with ...

Feb. 19, 2025 — Researchers have found a compound in ginger, called furanodienone (FDN), that selectively binds to and regulates a nuclear receptor involved in inflammatory bowel disease (IBD ...

BioMarin is a global biotechnology company focused on developing and commercializing therapies for rare genetic diseases. BioMarin specializes in enzyme replacement therapies, gene therapies, and ...

Environmental and lifestyle factors play a far greater role than genetics in determining the likelihood of dying young, according to the largest study yet to untangle the contributions of nature ...

The DWP Personal Independence Payments (PIP) can be claimed by those who suffer from a number of issues and you could get ...

BioMarin's gene therapy pipeline has had setbacks, including a three-year delay in US approval of Roctavian and stalled development of PKU gene therapy BMN 307 as the Food and Drug Administration ...

As of February 17, 2025, 1,028 unique patient prescriptions for Attruby™ have been written by 516 unique prescribers since FDA approval- ...

Genetics is the branch of science concerned with genes, heredity, and variation in living organisms. It seeks to understand the process of trait inheritance from parents to offspring, including ...

BioMarin Pharmaceutical exceeded earnings and revenue expectations in its Q4 2024 financial results.