It also significantly reduced plasma galactitol levels in adults and children with galactosemia. Additional studies provided strong efficacy and safety data across 185 classic galactosemia ...
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FDA extends review period for Applied Therapeutics’ govorestat NDAthe Phase I/II ACTION-Galactosemia study in adults; as well as preclinical findings. If approved, govorestat would become the first medication indicated for the treatment of galactosemia and aid ...
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