Total Revenue of $560 million, exceeding guidanceCrysvita® revenue of $410 million and Dojolvi® revenue of $88 million2025 Financial ...

This is one of 22 cutting-edge projects selected to share in a total of $8.1 million in grants raised through the Eagles ...

Dr. Eric Levine’s cutting-edge autism research at UConn School of Medicine is reprogramming the donated skin or blood cells of autism-linked Angelman or Dup15q syndrome patients to develop them in the ...

His research team has already shown there is a driver gene of UBE3A, which breaks down other cellular proteins in neurons, which can be either under- or overexpressed in the Angelman and Dup15q ...

The SOX9 gene locus is not only extensive but also intricate, and it could promote fibrosis in different organs or tissues, including cardiac fibrosis, liver fibrosis, kidney fibrosis, pulmonary ...

(MENAFN- PR Newswire) The team at UCLA is further developing this gene therapy approach in which a patient's own blood stem cells can be modified to add a healthy copy of the UBE3A gene that is ...

AUSTIN, Texas, Jan. 30, 2025 /PRNewswire/ -- Dr. Roger Hollis from the University of California, Los Angeles, project scientist from the laboratory of Dr. Donald Kohn, a world leader in ...

Donald Kohn, a world leader in developing gene replacement therapies using blood stem cells, has been awarded a $5.8 million translational research award from the California Institute for ...