Gene Therapy News -- ScienceDaily
2025年1月15日 · Read all about gene therapy including current medical research on switching therapeutic genes on and off, light-activated gene therapy and gene silencing.
Gene therapy - Latest research and news | Nature
2025年1月14日 · Gene therapy involves the introduction of new genes into cells, to restore or add gene expression, for the purpose of treating disease. Most commonly a mutated gene is replaced with DNA...
FDA approves first gene-editing treatment for human illness
2023年12月8日 · In a landmark decision, the Food and Drug Administration Friday approved the first gene-editing treatment to alleviate human illness. The FDA approved two gene therapies for anyone 12 and older...
FDA approves cure for sickle cell disease, the first ... - NBC News
The FDA on Friday also approved a second treatment for sickle cell disease, called Lyfgenia, a gene therapy from drugmaker Bluebird Bio. Both treatments work by genetically modifying a...
FDA Approves First Gene Therapies to Treat Patients with Sickle …
Today, the U.S. Food and Drug Administration approved two milestone treatments, Casgevy and Lyfgenia, representing the first cell-based gene therapies for the treatment of sickle cell disease...
The world's 1st CRISPR therapy has been approved. Here's …
2024年1月18日 · Drug regulators have approved a CRISPR therapy called Casgevy to treat inherited blood disorders. But what is it and how does it work?
'Will it really work?': Young sickle cell patient among the first to ...
Jason Kane / NBC News. ... Until the gene therapy, the only cure for sickle cell disease was a stem cell transplant from a donor. That worked for Wekem after Sylvia discovered she was a match for ...
RNA and epigenetic editing: The new frontier in gene and cell therapy
4 天之前 · Over the past two decades, the field of gene and cell therapy has been revolutionized by the advent of CRISPR-Cas9 genome editing.1,2 This technology has concomitantly driven the meteoric rise of the study of epigenetic and RNA editing, including m6A RNA methylation, m6A epitranscriptomics, and RNA-based editing methods. Indeed, thousands of articles focused on …
Gene therapy | AP News
2023年11月16日 · FDA approves 2 gene therapies for sickle cell. One is the first to use the editing tool CRISPR. A new cure for sickle cell disease may be coming. Health advisers will review it next week. Gene therapy eyedrops restored a boy’s sight. Similar treatments could help millions. Can gene therapy be harnessed to fight AIDS virus?
Gene Therapy News - BioPharma Dive
2025年1月7日 · Rapid scientific advances have put the gene therapy field at the forefront of biomedical research. But, as recent setbacks have shown, researchers and drugmakers still face major challenges. By BioPharma Dive staff